This website is intended for US residents only.

Brought to you by Zevra Therapeutics

Miplyffa
MIPLYFFA Now Approved

MIPLYFFA is the first FDA-approved treatment for Niemann-Pick disease type C (NPC)

AmplifyAssist™ - Your ally in what's ahead
Zevra is proud to introduce AmplifyAssist, a support program for caregivers and those living with NPC and taking MIPLYFFA.*
*For Eligible Patients
Clinical Education – Product and disease state information, including tips and tools for therapy management. The AmplifyAssist team does not offer medical advice or replace discussions with a healthcare provider.
Insurance Coverage Support – Help with understanding your insurance coverage, your options, and the steps to acquiring coverage for specialty medications.
Access Support - Assistance with identifying and enrolling eligible patients in financial support programs/services to help manage the cost of treatment
Prescription Fulfillment- Ongoing coordination of your prescription needs and deliveries
For Caregivers
Overview of MIPLYFFA
Download Caregiver Fact Sheet Download
To get started with MIPLYFFA,
please speak with your doctor.
For Healthcare Professionals
What to Know About MIPLYFFA
MIPLYFFA FACT SHEET Download
Getting Your Patients Started on MIPLYFFA
MIPLYFFA Prescription Enrollment Form Download
To learn more, call:
1-888-668-4198
Monday - Friday 8 am to 6 pm CT.
Stay in the know
Sign up for the latest information about MIPLYFFA and Niemann-Pick disease type C.

Now Approved

Now Approved

Which best describes you?(Required)

WHAT is MIPLYFFA [mye-plye’-fah]?

MIPLYFFA is prescription medicine used in combination with a drug called miglustat to treat neurological symptoms of Niemann-Pick disease type C (NPC) in patients 2 years of age and older.

IMPORTANT SAFETY INFORMATION

Before starting MIPLYFFA, tell your healthcare provider about all your medical conditions, including if you are pregnant or plan to become pregnant, breastfeeding or plan to breastfeed.

Tell your healthcare provider about all the medicines you take, including any prescription and over-the-counter medicines, vitamins, or herbal supplements. MIPLYFFA may affect how other medicines work.

What are the possible side effects of MIPLYFFA?

MIPLYFFA may cause serious side effects including:

  • Hypersensitivity reactions. Call your healthcare provider immediately if you get any of the following symptoms:
    • urticaria (hives),
    • shortness of breath,
    • persistent cough, or
    • facial swelling
  • Harm to your unborn baby. If you are of childbearing age, take precautions to prevent pregnancy. Tell your healthcare provider right away if you become pregnant or think you might be pregnant during treatment with MIPLYFFA.
  • Infertility. MIPLYFFA may affect your ability to have children.

The most common side effects of MIPLYFFA in patients also taking miglustat include upper respiratory tract infection, diarrhea and decreased weight.

These are not all the possible side effects of MIPLYFFA. Call your HCP for medical advice about side effects. You are encouraged to report side effects of prescription drugs to the FDA. Visit www.fda.gov/medwatch, or call 1-800-FDA-1088.

Drug Interactions: MIPLYFFA can cause side effects if used together with certain drugs called OCT2 substrates. Talk to your healthcare provider about any drugs that you may be taking for other conditions.

MIPLYFFA capsules for oral use are available in the following strengths in a 90-count bottle: 47 mg, 62 mg, 93 mg, and 124 mg.

For more information, please see the Prescribing Information, including Instructions for Use.

IMPORTANT SAFETY INFORMATION
Before starting MIPLYFFA, tell your healthcare provider about all your medical conditions, including if you are pregnant or plan to become pregnant, breastfeeding or plan to breastfeed. Tell your healthcare provider about all the medicines you take, including any prescription and over-the-counter medicines, vitamins, or herbal supplements. MIPLYFFA may affect how other medicines work.... Continue Reading